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Gene therapy rescues cilia defects and restores olfactory function in a mammalian ciliopathy model.
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Gene therapy rescues cilia defects and restores olfactory function in a mammalian ciliopathy model.
Gene therapy rescues cilia defects and restores olfactory function in a mammalian ciliopathy model. Nat Med. 2012 Sep; 18(9):1423-8.
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PubMed
subject areas
Adenoviridae
Animals
Cilia
Genetic Complementation Test
Genetic Diseases, Inborn
Genetic Therapy
Genetic Vectors
Humans
Mice
Microscopy, Fluorescence
Mutation
Olfactory Receptor Neurons
Smell
Tubulin
Tumor Suppressor Proteins
Zebrafish
authors with profiles
RICHARD GIBBS
DONNA MUZNY
ANIKO SABO